| Manufacturer ▼ | Drug Name | Indication | Stage | Status | Route of Administration | Drug Class |
|---|---|---|---|---|---|---|
| Prothena Corporation plc | Prasinezumab (PRX002) | Parkinson's disease | Phase 3 | Ongoing | Intravenous | Neurology |
| Prothena Corporation plc | NEOD001 PRONTO | Previously-treated patients with AL amyloidosis and persistent cardiac dysfunction | Phase 2b | Trial Discontinued | Intravenous | Cardiology |
| Prothena Corporation plc | BMS-986446 (PRX005) - (TargetTau-1) | Alzheimer’s disease | Phase 2 | Ongoing | Intravenous | Neurology |
| Psyence Biomedical Ltd. | Psilocybin (NPX5) | Adjustment Disorder due to a recent cancer diagnosis | Phase 2b | Enrollment Initiation | Oral | Psychiatric |
| Psyence Biomedical Ltd. | CLA-PSY-201 | Alcohol Use Disorder (AUD) | Phase 2b | Ongoing | Oral | Psychiatric |
| PTC Therapeutics Inc. | Translarna (ataluren) - (041) | Duchenne muscular dystrophy caused by nonsense mutations (nmDMD) | PDUFA | Ongoing | Oral | Genetic Disorder |
| PTC Therapeutics Inc. | Upstaza | Gene therapy | BLA Filing | Trial Planned | Intracerebral | Genetic Disorder |
| PTC Therapeutics Inc. | Translarna | Nonsense mutation cystic fibrosis | Phase 3 | Trial Discontinued | Oral | Genetic Disorder |