Pipeline Report

Updated February 1st, 2026

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Showing results 3,393–3,400 of 4,419
Manufacturer ▼ Drug Name Indication Stage Status Route of Administration Drug Class
Protalix BioTherapeutics Inc. (DE) Pegunigalsidase alfa Fabry disease Phase 3 Trial Completed Intravenous Genetic Disorder
Protalix BioTherapeutics Inc. (DE) Pegunigalsidase alfa (PRX-102) - (BALANCE) Fabry disease Phase 3 Data Released Intravenous Genetic Disorder
Protalix BioTherapeutics Inc. (DE) PRX-115 Severe Gout Phase 2 Trial Planned Intravenous Orthopedic
Protara Therapeutics Inc. TARA-002 Lymphatic Malformations (LMs) Phase 3 Trial Planned Intravesical N/A
Protara Therapeutics Inc. TARA-002 Lymphatic Malformations (LMs) Phase 3 Trial Planned Intravesical N/A
Protara Therapeutics Inc. TARA-002 - (STARBORN-1) Pediatric patients with lymphatic malformations (LMs) Phase 2 Data Released Intravesical N/A
Prothena Corporation plc Coramitug (PRX004) - (CLEOPATTRA) ATTR-cardiomyopathy Phase 3 Ongoing intravenous Cardiology
Prothena Corporation plc Birtamimab - (AFFIRM-AL) AL Amyloidosis Phase 3 Trial Discontinued Intravenous Hematology