Pipeline Report

Updated February 1st, 2026

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Showing results 417–424 of 4,419
Manufacturer ▼ Drug Name Indication Stage Status Route of Administration Drug Class
Amylyx Pharmaceuticals Inc. AMX0035 - (HELIOS) Wolfram Syndrome Phase 2 Data Released Oral Genetic Disorder
Amylyx Pharmaceuticals Inc. AMX0035 - (A35-004 PHOENIX) Amyotrophic Lateral Sclerosis (AML) Phase 3 Trial Discontinued Oral Neurology
Amylyx Pharmaceuticals Inc. RELYVRIO (sodium phenylbutyrate and taurursodiol) Amyotrophic lateral sclerosis (ALS) Phase 3 Withdrawn oral Neurology
Amylyx Pharmaceuticals Inc. AMX0035 - (PEGASUS) Alzheimer's Disease Phase 2 Data Released oral Neurology
AN2 Therapeutics Inc. EBO-301 Treatment-Refractory MAC Lung Disease Phase 3 Trial Completed Intravenous Respiratory
AN2 Therapeutics Inc. Epetraborole Melioidosis Phase 2 Trial Planned Oral Antibiotic
AN2 Therapeutics Inc. Epetraborole - (EBO-103) Mycobacterium avium complex (MAC) lung disease, Chronic non-tuberculous mycobacterial (NTM) lung disease Phase 2/3 Data Released Oral Respiratory
AnaptysBio Inc. Jemperli (dostarlimab) plus chemotherapy - (PERLA) Non-squamous non-small cell lung cancer (NSCLC) Phase 2 Trial Completed Intravenous Oncology