Pipeline Report

Updated February 1st, 2026

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You attempted to open: Drug Pipeline Report
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Showing results 4,225–4,232 of 4,419
Manufacturer ▼ Drug Name Indication Stage Status Route of Administration Drug Class
Vertex Pharmaceuticals Incorporated VX-407 Autosomal Dominant Polycystic Kidney Disease (ADPKD), healthy volunteers Phase 2 Enrollment Initiation oral Genetic Disorder
Vertex Pharmaceuticals Incorporated VX-993 Painful diabetic peripheral neuropathy (DPN) Phase 2 Enrollment Initiation Intravenous Neurology
Vertex Pharmaceuticals Incorporated VX-993 Moderate to severe acute pain Phase 2 Trial Discontinued Intravenous Non-Opioid Analgesic
Vertex Pharmaceuticals Incorporated VX-864 Alpha-1 Antitrypsin Deficiency (AATD) Phase 2 Ongoing Oral Genetic Disorder
Vertex Pharmaceuticals Incorporated Suzetrigine (VX-548) Painful diabetic peripheral neuropathy (DPN) Phase 2 Ongoing Oral Neurology
Vertex Pharmaceuticals Incorporated VX-864 Alpha-1 antitrypsin (AAT) deficiency Phase 2 Trial Discontinued Oral Genetic Disorder
Vertex Pharmaceuticals Incorporated VX-147 Focal segmental glomerulosclerosis (FSGS) Phase 2 Trial Completed oral #N/A
Vertex Pharmaceuticals Incorporated VX-814 alpha-1 antitrypsin (AAT) deficiency Phase 2 Trial Discontinued Oral Genetic Disorder