Pipeline Report

Updated February 1st, 2026

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Showing results 3,825–3,832 of 4,419
Manufacturer ▼ Drug Name Indication Stage Status Route of Administration Drug Class
Sanofi Rilzabrutinib (PRN1008) IgG4-related disease (IgG4-RD) Phase 2 Ongoing Oral Immunology
Sanofi PRV-3279 - (PREVAIL-2) Systemic Lupus Erythematosus (SLE) and Lupus nephritis (LN) Phase 2a Ongoing Intravenous Immunology
Sanofi PRV-6527 Crohn's disease Phase 2a Trial Discontinued Oral Gastroenterology
Sarepta Therapeutics Inc. SRP-9003-301 - (EMERGENE) Limb-girdle muscular dystrophy type 2E (LGMD2E) BLA Filing Ongoing Intravenous Genetic Disorder
Sarepta Therapeutics Inc. SRP-4045 + SRP-4053 (ESSENCE) Duchenne muscular dystrophy Phase 3 Data Released Intravenous Genetic Disorder
Sarepta Therapeutics Inc. LYS-SAF302 Mucopolysaccharidosis type IIIA (MPS IIIA) Phase 2/3 Ongoing Intracerebral Genetic Disorder
Sarepta Therapeutics Inc. SRP-9001-102 Duchenne muscular dystrophy Phase 2 Data Released Intravenous Genetic Disorder
Sarepta Therapeutics Inc. SRP-5051 - (MOMENTUM) Duchenne muscular dystrophy Phase 2 Data Released Intravenous Genetic Disorder