Pipeline Report

Updated February 1st, 2026

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Showing results 3,369–3,376 of 4,419
Manufacturer ▼ Drug Name Indication Stage Status Route of Administration Drug Class
ProKidney Corp. REGEN-016 - (PROACT 2) Type 2 Diabetes Phase 3 Trial Discontinued Intravenous Endocrinology
ProKidney Corp. Rilparencel - (REGEN-007) Diabetic CKD Stage 3/4 Phase 2 Data Released Oral Endocrinology
ProKidney Corp. RMCL-002 - (REACT) Type 2 diabetes, prevent/delay CKD Phase 2 Data Released Intravenous Endocrinology
ProKidney Corp. REGEN-003 Type 2 Diabetes Phase 2 Trial Completed Intravenous Endocrinology
ProQR Therapeutics N.V. QR-421a - (Sirius) Retinitis Pigmentosa Phase 2/3 Trial Discontinued Intravitreal injection Genetic Disorder
ProQR Therapeutics N.V. QR-421a - (Celeste) Usher Syndrome Type 2 Phase 2/3 Ongoing Intravitreal Genetic Disorder
ProQR Therapeutics N.V. Sepofarsen (QR-110) - (ILLUMINATE) Leber's Congenital Amaurosis (LCA) - Genetic blindness Phase 2/3 Trial Discontinued Intravitreal injection Genetic Disorder
ProQR Therapeutics N.V. QR-421a - (Helia) Retinitis pigmentosa Phase 2 Trial Discontinued Intravitreal injection Genetic Disorder