Pipeline Report

Updated February 1st, 2026

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Showing results 281–288 of 4,419
Manufacturer ▼ Drug Name Indication Stage Status Route of Administration Drug Class
Alnylam Pharmaceuticals Inc. Nucresiran Hereditary Transthyretin Amyloidosis with Polyneuropathy (hATTR-PN) Phase 3 Trial Planned Intravenous Genetic Disorder
Alnylam Pharmaceuticals Inc. Vutrisiran - (HELIOS-A) ATTR Amyloidosis Phase 3 Data Released Subcutaneous Genetic Disorder
Alnylam Pharmaceuticals Inc. Mivelsiran - (cAPPricorn-1) Cerebral amyloid angiopathy Phase 2 Ongoing Subcutaneous Neurology
Alnylam Pharmaceuticals Inc. ALN-4324 Type 2 diabetes Phase 2 Trial Planned Intravenous Endocrinology
Alnylam Pharmaceuticals Inc. Nucresiran (ALN-TTRsc04) - (TRITON-CM) ATTR amyloidosis Phase 3 Ongoing Subcutaneous Genetic Disorder
Alnylam Pharmaceuticals Inc. Vutrisiran - (HELIOS-B) ATTR Amyloidosis with Cardiomyopathy (ATTR-CM) Phase 3 Data Released Subcutaneous Cardiology
Alnylam Pharmaceuticals Inc. Zilebesiran - (ZENITH CVOT) Major adverse cardiovascular (CV) events Phase 3 Ongoing Subcutaneous Cardiology
Alpha Tau Medical Ltd. Alpha DaRT - (IMPACT) Pancreatic ductal adenocarcinoma (PDAC) Phase 3 Intratumoral Oncology