| Manufacturer ▼ | Drug Name | Indication | Stage | Status | Route of Administration | Drug Class |
|---|---|---|---|---|---|---|
| Agios Pharmaceuticals Inc. | Mitapivat (AG-348) - (RISE UP) | Sickle cell disease | Phase 3 | Data Released | Oral | Hematology |
| Agios Pharmaceuticals Inc. | AG-120 and VIDAZA - (AGILE) | Frontline Acute myeloid leukemia (AML) harboring an IDH1 mutation - cancer | Phase 3 | Trial Completed | Oral and subcutaneous | Oncology |
| Agios Pharmaceuticals Inc. | Vorasidenib (AG-881) | Glioma | Phase 3 | Withdrawn | Oral | Oncology |
| Agios Pharmaceuticals Inc. | Mitapivat (AG-348) - (ACTIVATE-T) | Pyruvate Kinase Deficiency | Phase 3 | Ongoing | Oral | Genetic Disorder |
| Agios Pharmaceuticals Inc. | Mitapivat (AG-348) - (RISE UP) | Sickle cell disease | Phase 3 | Data Released | Oral | Hematology |
| Agios Pharmaceuticals Inc. | Mitapivat (AG-348) - (RISE UP) | Sickle cell disease | Phase 3 | Data Released | Oral | Hematology |
| Agios Pharmaceuticals Inc. | Mitapivat (AG-348) - (ACTIVATE-T) | Pyruvate Kinase Deficiency | Phase 3 | Ongoing | Oral | Genetic Disorder |
| Agios Pharmaceuticals Inc. | TIBSOVO (ivosidenib) - (ClarIDHy) | IDH1 mutant cholangiocarcinoma - cancer | sNDA Filing | Trial Completed | oral | Oncology |