Pipeline Report

Updated February 1st, 2026

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Showing results 985–992 of 4,419
Manufacturer ▼ Drug Name Indication Stage Status Route of Administration Drug Class
BioLineRx Ltd. Motixafortide (BL-8040) and KEYTRUDA (pembrolizumab) Pancreatic cancer Phase 2a Trial Discontinued Motixafortide subcutaneous KEYTRUDA intravenous Oncology
BioLineRx Ltd. Motixafortide (BL-8040) - BLAST Consolidation treatment for AML cancer patients Phase 2b Trial Discontinued Subcutaneous Oncology
BioMarin Pharmaceutical Inc. PALYNZIQ (pegvaliase-pqpz) - (PEGASUS) Phenylketonuria (PKU) in adolescents aged 12-17 PDUFA priority review Ongoing Subcutaneous Genetic Disorder
BioMarin Pharmaceutical Inc. VOXZOGO Hypochondroplasia Phase 3 Ongoing Subcutaneous Genetic Disorder
BioMarin Pharmaceutical Inc. BMN 401 (INZ-701) - (ENERGY-2) ENPP1 Deficiency Phase 3 Trial Planned Subcutaneous Genetic Disorder
BioMarin Pharmaceutical Inc. Valoctocogene roxaparvovec (BMN 270-303) - (GENEr8-3) Hemophilia A Phase 3 Ongoing Intravenous Hematology
BioMarin Pharmaceutical Inc. BMN 401 (INZ-701) ABCC6 deficiency Phase 3 Trial Planned Subcutaneous Genetic Disorder
Biomea Fusion Inc. Icovamenib (BMF-219) with a GLP-1-Based Therapy - (COVALENT-211) Diabetes and obesity Phase 2b Trial Planned Oral Endocrinology