Pipeline Report

Updated February 1st, 2026

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Showing results 4,217–4,224 of 4,419
Manufacturer ▼ Drug Name Indication Stage Status Route of Administration Drug Class
Vertex Pharmaceuticals Incorporated inaxaplin (VX-147) - (AMPLITUDE) Proteinuric kidney disease with two mutations in the APOL1 gene (AMKD) Phase 3 Ongoing oral Genetic Disorder
Vertex Pharmaceuticals Incorporated VX-661 Cystic fibrosis - one copy of the F508del mutation and a second mutation that results in minimal CFTR Function Phase 3 Trial Discontinued oral Genetic Disorder
Vertex Pharmaceuticals Incorporated VX-121/tezacaftor/VX-561 - (SKYLINE-102) Cystic Fibrosis Phase 3 Ongoing Oral Respiratory
Vertex Pharmaceuticals Incorporated VX-661 Cystic fibrosis - one copy of the F508del mutation and a second mutation that results in minimal CFTR Function Phase 3 Trial Discontinued oral Genetic Disorder
Vertex Pharmaceuticals Incorporated VX-121/tezacaftor/VX-561 - (SKYLINE-102) Cystic Fibrosis Phase 3 Ongoing Oral Respiratory
Vertex Pharmaceuticals Incorporated Suzetrigine Painful Lumbosacral Radiculopathy Phase 3 Trial Planned Oral Orthopedic
Vertex Pharmaceuticals Incorporated Povetacicept - (OLYMPUS) Primary Membranous Nephropathy (pMN) Phase 2/3 Ongoing Subcutaneous Immunology
Vertex Pharmaceuticals Incorporated Povetacicept Generalized myasthenia gravis Phase 2 Trial Planned Subcutaneous Neurology