Pipeline Report

Updated February 1st, 2026

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Showing results 3,961–3,968 of 4,419
Manufacturer ▼ Drug Name Indication Stage Status Route of Administration Drug Class
Syros Pharmaceuticals Inc. Tamibarotene (SY-1425) and VIDAZA (azaciditine) - (SELECT-MDS-1) Myelodysplastic Syndrome Phase 3 Trial Discontinued Oral and subcutaneous Hematology
Syros Pharmaceuticals Inc. SY-2101 Acute Promyelocytic Leukemia (APL) Phase 3 Trial Discontinued Oral Oncology
Syros Pharmaceuticals Inc. Tamibarotene (SY-1425) with VENCLEXTA (venetoclax) and VIDAZA (azacitidine) - (SELECT-AML-1) Acute myeloid leukemia (AML) Phase 2 Data Released Oral Oncology
Takeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of) Fazirsiran (TAK-999/ARO-AAT) - (REDWOOD) Alpha-1 antitrypsin deficiency (AATD-LD) NDA Filing Data Released Intravenous Genetic Disorder
Takeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of) Rusfertide - (VERIFY) Polycythemia vera NDA Filing Ongoing Subcutaneous Hematology
Takeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of) Rusfertide - (VERIFY) Polycythemia vera NDA Filing Ongoing Subcutaneous Hematology
Takeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of) QDENGA (TAK-003) - (TIDES) Dengue Vaccine NDA Filing Withdrawn Subcutaneous Immunology
Takeda Pharmaceutical Company Limited American Depositary Shares (each representing 1/2 of a share of) Oveporexton (TAK-861-2001) Narcolepsy type 1 (NT1) NDA Filing Data Released Oral Neurology