Pipeline Report

Updated February 1st, 2026

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Showing results 185–192 of 4,419
Manufacturer ▼ Drug Name Indication Stage Status Route of Administration Drug Class
Agios Pharmaceuticals Inc. AG-120 and VIDAZA - (AGILE) Frontline Acute myeloid leukemia (AML) harboring an IDH1 mutation - cancer Phase 3 Trial Completed Oral and subcutaneous Oncology
Agios Pharmaceuticals Inc. Mitapivat (AG-348) - (ESTIMATE Open Label) Sickle Cell Disease Phase 2 Ongoing Oral Hematology
Agios Pharmaceuticals Inc. AG-946 Myelodysplastic syndrome (MDS) Phase 2a Ongoing oral Hematology
Agios Pharmaceuticals Inc. Mitapivat (AG-348) - (RISE UP) Sickle cell disease Phase 3 Data Released Oral Hematology
Agios Pharmaceuticals Inc. Mitapivat - (SATISFY) Erythrocyte Membranopathies and Congenital Dyserythropoietic Anemia Type II Phase 2 Ongoing Oral Hematology
Agios Pharmaceuticals Inc. Mitapivat (AG-348) - (ACTIVATE kids-T study) Pediatric PK Deficiency Phase 3 Data Released Oral Genetic Disorder
Agios Pharmaceuticals Inc. TIBSOVO (ivosidenib) - (ClarIDHy) IDH1 mutant cholangiocarcinoma - cancer sNDA Filing Trial Completed oral Oncology
AIM ImmunoTech Inc. Ampligen, Intron A, and celecoxib Colorectal cancer Phase 2 Ampligen intravenous Intron A subcutaneous intramuscular intravenous celecoxib oral Oncology