Pipeline Report

Updated February 1st, 2026

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Showing results 1,225–1,232 of 4,419
Manufacturer ▼ Drug Name Indication Stage Status Route of Administration Drug Class
CASI Pharmaceuticals Inc. CNCT19 (CD19 CAR-T) - (B-NHL) Non-Hodgkin Lymphoma (NHL) / Acute lymphoblastic leukemia (ALL) Phase 2 Enrollment Initiation Intravenous Oncology
Cassava Sciences Inc. Simufilam (PTI-125) - (REFOCUS-ALZ) Mild-to-Moderate Alzheimer's Disease Phase 3 Trial Discontinued Oral Neurology
Cassava Sciences Inc. Simufilam (PTI-125-04) Alzheimer's Disease Phase 3 Trial Discontinued Oral Neurology
Cassava Sciences Inc. Simufilam (PTI-125) - (RETHINK-ALZ) Alzheimer’s disease Phase 3 Trial Discontinued Oral Neurology
Cassava Sciences Inc. Simufilam - (CMS) Alzheimer's disease Phase 3 Ongoing Oral Neurology
Catalyst Pharmaceuticals Inc. FIRDAPSE (amifampridine) Spinal Muscular Atrophy (SMA) Type 3 Phase 2 Trial Discontinued oral Genetic Disorder
CDT Equity Inc. AZD1656 Renal Transplant Phase 2 Trial Planned oral Immunosuppressant
CDT Equity Inc. AZD1656 Systemic lupus erythematosus (including lupus nephritis) Phase 2a Trial Planned oral Immunology